Nathan E Botts / Monday, April 26, 2021 / Categories: Mental Health NIMH Workshop: Gene-based Therapeutics for Rare Genetic Neurodevelopmental Psychiatric Disorders NIMH Workshop: Gene-based Therapeutics for Rare Genetic Neurodevelopmental Psychiatric DisordersOn January 21, 2021, the National Institute of Mental Health (NIMH) conducted a virtual workshop that provided insights into the potential challenges and opportunities for gene-based therapeutic strategies for individuals with rare genetic neurodevelopmental disorders. This workshop brought together a multi-disciplinary group of experts from academia, government, and industry to provide a review of the current state of science in gene-targeted therapeutics and characteristics of suitable gene/molecular targets and mechanisms amenable to gene-based therapies. This workshop also featured some of the gene-targeted approaches that are currently in the clinic or in development to highlight the scientific rationale for each treatment and the milestones for reaching key stages of therapeutics development, and the challenges and lessons learned along the way.Link to original article Previous Article NIMH Director’s Innovation Speaker Series: Advancing Therapies for Central Nervous System Disorders Next Article Getting to Know Your Brain: Dealing with Stress Print 168 Rate this article: No rating 0Upvote 0Downvote Leave a comment Name: Please enter a name. Email: Please enter an email address. Please enter a valid email address. Comment: Please enter comment. Add comment